
23/09/2025
The FDA doesn’t hand out gold stars often, but one rare disease therapy just got fast-tracked. Could this be the first-ever U.S. treatment approval for LHON?
The countdown to February 28, 2026 is officially on… Get all caught up here: https://piemagazine.org/fda-idebenone-leber-hereditary-optic-neuropathy/
A rare disease, a rare chance. FDA fast-tracks idebenone for LHON. The U.S. Food and Drug Administration (FDA) doesn’t hand...