10/23/2025
This was a special one.
Not only is Sophia a powerful and fearless voice of advocacy for Huntington's Disease, but while we were in the middle of editing, uniQure made headlines.
Their positive top-line results from the Phase I/II trial of AMT-130 in Huntington's are a milestone in the evolution of gene therapy, and we are honored to help share this important story.
Sophia, a Huntington's disease patient advocate based in Germany, shares her experience living with Huntington's disease and her hope for a brighter future a...